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story of the week
Published in Neurology

Journal Scan / Research · August 26, 2020

Viltolarsen Treatment in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping

JAMA Neurology


Additional Info

JAMA Neurology
Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial
JAMA Neurol 2020 Aug 01;77(8)982-991, PR Clemens, VK Rao, AM Connolly, AD Harper, JK Mah, EC Smith, CM McDonald, CM Zaidman, LP Morgenroth, H Osaki, Y Satou, T Yamashita, EP Hoffman

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.

Further Reading