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Published in Neurology

Journal Scan / Research · October 15, 2020

Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With DMD

JAMA Neurology


Additional Info

JAMA Neurology
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial
JAMA Neurol 2020 Sep 01;7(9)1122-1131, JR Mendell, Z Sahenk, K Lehman, C Nease, LP Lowes, NF Miller, MA Iammarino, LN Alfano, A Nicholl, S Al-Zaidy, S Lewis, K Church, R Shell, LH Cripe, RA Potter, DA Griffin, E Pozsgai, A Dugar, M Hogan, LR Rodino-Klapac

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.

Further Reading