Long-Term Safety and Efficacy of Avalglucosidase-α in Patients With Late-Onset Pompe Disease
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Neurology
From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.
Long-term Safety and Efficacy of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease
Neurology 2022 Aug 02;99(5)e536-e548, MM Dimachkie, RJ Barohn, B Byrne, O Goker-Alpan, PS Kishnani, S Ladha, P Laforêt, KE Mengel, LDM Peña, S Sacconi, V Straub, J Trivedi, P Van Damme, AT van der Ploeg, J Vissing, P Young, KA Haack, M Foster, JM Gilbert, P Miossec, O Vitse, T Zhou, B SchoserFrom MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.