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Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy
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The New England Journal of Medicine
From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.
Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy
N. Engl. J. Med 2024 Oct 10;391(14)1302-1312, F Eichler, CN Duncan, PL Musolino, TC Lund, AO Gupta, S De Oliveira, AJ Thrasher, P Aubourg, JS Kühl, DJ Loes, H Amartino, N Smith, J Folloni Fernandes, C Sevin, R Sankar, SA Hussain, P Gissen, JH Dalle, U Platzbecker, GF Downey, E McNeil, L Demopoulos, AC Dietz, HL Thakar, PJ Orchard, DA WilliamsFrom MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.