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story of the week
Published in Benign Hematology

Journal Scan / Research · April 25, 2019

Lentiviral Gene Therapy Combined With Low-Dose Busulfan in Infants With SCID-X1

The New England Journal of Medicine

 

Additional Info

Disclosure statements are available on the authors' profiles:

The New England Journal of Medicine
Lentiviral Gene Therapy Combined With Low-Dose Busulfan in Infants With SCID-X1
N. Engl. J. Med 2019 Apr 18;380(16)1525-1534, E Mamcarz, S Zhou, T Lockey, H Abdelsamed, SJ Cross, G Kang, Z Ma, J Condori, J Dowdy, B Triplett, C Li, G Maron, JC Aldave Becerra, JA Church, E Dokmeci, JT Love, AC da Matta Ain, H van der Watt, X Tang, W Janssen, BY Ryu, SS De Ravin, MJ Weiss, B Youngblood, JR Long-Boyle, S Gottschalk, MM Meagher, HL Malech, JM Puck, MJ Cowan, BP Sorrentino

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.

Further Reading