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Published in Neurology

Journal Scan / Research · December 10, 2021

Hematopoietic Stem Cell and Progenitor Cell Gene Therapy for Hurler Syndrome

The New England Journal of Medicine


Additional Info

The New England Journal of Medicine
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome
N. Engl. J. Med 2021 Nov 18;385(21)1929-1940, B Gentner, F Tucci, S Galimberti, F Fumagalli, M De Pellegrin, P Silvani, C Camesasca, S Pontesilli, S Darin, F Ciotti, M Sarzana, G Consiglieri, C Filisetti, G Forni, L Passerini, D Tomasoni, D Cesana, A Calabria, G Spinozzi, MP Cicalese, V Calbi, M Migliavacca, F Barzaghi, F Ferrua, V Gallo, S Miglietta, E Zonari, PS Cheruku, C Forni, M Facchini, A Corti, M Gabaldo, S Zancan, S Gasperini, A Rovelli, JJ Boelens, SA Jones, R Wynn, C Baldoli, E Montini, S Gregori, F Ciceri, MG Valsecchi, G la Marca, R Parini, L Naldini, A Aiuti, ME Bernardo

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.

Further Reading